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Niemann-Pick Disease Type C1

Niemann-Pick Disease Type C1

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Niemann-Pick Disease Type C1: Understanding the Symptoms, Causes, Diagnosis, Treatment, and More Introduction Niemann-Pick Disease Type C1 (NP-C1) is a rare, progressive genetic disorder characterized by the abnormal accumulation of lipids (fats) within the body’s cells. This buildup leads to a wide range of symptoms that can affect multiple organ systems, including the brain. NP-C1…